| タイトル |
Open-label clinical trial of bezafibrate treatment in patients with fatty acid oxidation disorders in Japan; 2nd report QOL survey
|
| 著者 |
Shiraishi Hideaki
Oki Eishin
Ishige Mika
Fukao Toshiyuki
Hamada Yusuke
Sakai Norio
Ochi Fumihiro
Watanabe Asami
Kawakami Sanae
Kuzume Kazuyo
Watanabe Kenji
Sameshima Koji
Nakamagoe Kiyotaka
Tamaoka Akira
Asahina Naoko
Yokoshiki Saki
Miyakoshi Takashi
Oba Koji
Isoe Toshiyuki
Hayashi Hiroshi
Sato Norihiro
|
| 収録物名 |
MOLECULAR GENETICS AND METABOLISM REPORTS
|
| 巻 | 20 |
| 収録物識別子 |
EISSN 2214-4269
|
| 主題 |
Bezafibrate; Fatty acid oxidation disorders (FAODs); Very long-chain acyl-CoA dehydrogenase (VLCAD) deficiency; Carnitine palmitoyltransferase-II (CPT-2) deficiency; Clinical trial; Quality of life
|
| 言語 |
英語
|
| 資源タイプ | 学術雑誌論文 |
| 出版者 |
ELSEVIER
|
| 発行日 | 2019-09 |
| アクセス権 | メタデータのみ |
| 関連情報 |
[DOI] 10.1016/j.ymgmr.2019.100496
[PMID] 31372341
|
| 備考 | This study was supported by The multicenter clinical trial of the efficacy and safety of bezafibrate for mitochondrial fatty acid beta-oxidation disorders (Grant Number, 16lk0103005h0005) from the Japan Agency for Medical Research and Development (AMED). |
