| Title |
Open-label clinical trial of bezafibrate treatment in patients with fatty acid oxidation disorders in Japan; 2nd report QOL survey
|
| Creator |
Shiraishi Hideaki
Oki Eishin
Ishige Mika
Fukao Toshiyuki
Hamada Yusuke
Sakai Norio
Ochi Fumihiro
Watanabe Asami
Kawakami Sanae
Kuzume Kazuyo
Watanabe Kenji
Sameshima Koji
Nakamagoe Kiyotaka
Tamaoka Akira
Asahina Naoko
Yokoshiki Saki
Miyakoshi Takashi
Oba Koji
Isoe Toshiyuki
Hayashi Hiroshi
Sato Norihiro
|
| Source Title |
MOLECULAR GENETICS AND METABOLISM REPORTS
|
| Volume | 20 |
| Journal Identifire |
EISSN 2214-4269
|
| Subjects |
Bezafibrate; Fatty acid oxidation disorders (FAODs); Very long-chain acyl-CoA dehydrogenase (VLCAD) deficiency; Carnitine palmitoyltransferase-II (CPT-2) deficiency; Clinical trial; Quality of life
|
| Language |
eng
|
| Resource Type | journal article |
| Publisher |
ELSEVIER
|
| Date of Issued | 2019-09 |
| Access Rights | metadata only access |
| Relation |
[DOI] 10.1016/j.ymgmr.2019.100496
[PMID] 31372341
|
| Remark | This study was supported by The multicenter clinical trial of the efficacy and safety of bezafibrate for mitochondrial fatty acid beta-oxidation disorders (Grant Number, 16lk0103005h0005) from the Japan Agency for Medical Research and Development (AMED). |
