Open-label clinical trial of bezafibrate treatment in patients with fatty acid oxidation disorders in Japan

MOLECULAR GENETICS AND METABOLISM REPORTS Volume 15 Page 55-63 published_at 2018-06
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Title
Open-label clinical trial of bezafibrate treatment in patients with fatty acid oxidation disorders in Japan
Creator
Shiraishi Hideaki
Oki Eishin
Ishige Mika
Fukao Toshiyuki
Hamada Yusuke
Sakai Norio
Ochi Fumihiro
Watanabe Asami
Kawakami Sanae
Kuzume Kazuyo
Watanabe Kenji
Sameshima Koji
Nakamagoe Kiyotaka
Tamaoka Akira
Asahina Naoko
Yokoshiki Saki
Miyakoshi Takashi
Ono Kota
Oba Koji
Isoe Toshiyuki
Hayashi Hiroshi
Sato Norihiro
Source Title
MOLECULAR GENETICS AND METABOLISM REPORTS
Volume 15
Start Page 55
End Page 63
Journal Identifire
ISSN 2214-4269
Subjects
Bezafibrate; Fatty acid oxidation disorders (FAODs); Very long-chain acyl-CoA dehydrogenase (VLCAD) deficiency; Carnitine palmitoyltransferase-II (CPT-2) deficiency; Clinical trial ( Other)
Language
eng
Resource Type journal article
Publisher
ELSEVIER SCIENCE BV
Date of Issued 2018-06
Access Rights metadata only access
Relation
[DOI] 10.1016/j.ymgmr.2018.02.003
[PMID] 29552494
Remark This study was supported by The multicenter clinical trial of the efficacy and safety of bezafibrate for mitochondrial fatty acid beta-oxidation disorders (Grant Number, 16lk0103005h0005) from the Japan Agency for Medical Research and Development (AMED).